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Neuromuscular

About this condition
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News

05.11.20

Pegunigalsidase Improved Renal Function in Fabry Disease in Phase 3 Clinical Trial
  • KEYWORDS:
  • Fabry disease
  • Neuromuscular disease
  • pegunigalsidase

News

04.30.20

EMA Recommends Orphan Drug Designation for Tauroursodeoxycholic Acid/Sodium Phenylbutyrate for ALS
  • KEYWORDS:
  • Amyotrophic Lateral Sclerosis
  • Neuromuscular disease
Neuromuscular Notes: Next Generation Treatments for Myasthenia Gravis image

Columns

Neuromuscular Notes: Next Generation Treatments for Myasthenia Gravis

Complement inhibitors, FcRn antagonists, and B-cell targeted therapies increase treatment options for MG but do not replace existing immunosuppressive therapies.

Leeann B. Burton, MD, and Amanda C. Guidon, MD

News

04.23.20

May 1 Facebook Live Session on ALS Sponsored by Muscular Dystrophy Association
  • KEYWORDS:
  • Amyotrophic Lateral Sclerosis
  • Neuromuscular disease

News

04.22.20

FDA Grants Fast Track Designation to Vutrisiran for Treatment of hATTR Amyloidosis in Adults
  • KEYWORDS:
  • Inherited neuropathy
  • Neuromuscular disease
  • Neuropathy
  • Polyneuropathy
  • vutrisiran

News

04.17.20

Muscular Dystrophy Association Launches Survey to Prioritize Needs During Pandemic
  • KEYWORDS:
  • Coronavirus
  • COVID-19
  • Muscular dystrophy
  • Neuromuscular disease

News

04.09.20

FDA Extends Date for Review of Risdiplam New Drug Application for SMA
  • KEYWORDS:
  • Risdiplam
  • Spinal muscular atrophy

News

04.03.20

First Patient Treated with Higher Dose of Nusinersen in Phase 2/3 Clinical Trial Study
  • KEYWORDS:
  • Neuromuscular disease
  • Nusinersen
  • Spinal muscular atrophy

News

03.24.20

Investigational Nonsteroidal Edaslonexent Treatment for Duchenne Muscular Dystrophy
  • KEYWORDS:
  • Duchenne muscular dystrophy
  • Edaslonexent
  • MDA Annual Meeting 2020
  • Neuromuscular disease

News

03.24.20

Autologous Transplant of Proinflammatory T-Cells Slows Amyotrophic Lateral Sclerosis
  • KEYWORDS:
  • Amyotrophic Lateral Sclerosis
  • Autologous Treg cells
  • MDA Annual Meeting 2020

News

03.24.20

Signals of Efficacy Seen With Onasemnogene Therapy for Spinal Muscular Atrophy Type 2
  • KEYWORDS:
  • MDA Annual Meeting 2020
  • Onasemnogene-parvovec
  • Spinal muscular atrophy

News

03.24.20

Eculizumab May Have Efficacy for Treatment of Myasthenia Gravis With Longer Treatment Period
  • KEYWORDS:
  • Eculizumab
  • MDA Annual Meeting 2020
  • Myasthenia gravis

News

03.20.20

Registration Available for Neuropathy Action Awareness Day
  • KEYWORDS:
  • Coronavirus
  • COVID-19
  • Neuropathy
Peripheral Neuropathy Caused by Vitamin B12 Deficiency image

Case Report

Peripheral Neuropathy Caused by Vitamin B12 Deficiency

Vitamin B12-deficiency was precipitated by nitrous oxide in a child with autism.

Vishnu Anand Cuddapah, MD, PhD; Susan Matesanz, MD; Sabrina W. Yum, MD; Brenda L. Banwell, MD; and Donna Stephenson, MD

Medical Transition from Pediatric to Adult Care in Neurology image

Cover Focus

Medical Transition from Pediatric to Adult Care in Neurology

It is critical to see transition as a process not simply a moment in time when care is transferred.

Lawrence W. Brown, MD

This Month's Issue
Idiopathic Intracranial Hypertension

Karissa N. Arca, MD, and Amaal J. Starling, MD

Diagnosing Secondary Headaches

Chia-Chun Chiang, MD, and Juliana VanderPluym, MD, FRCP, FAHS